P

I understand your point but u are bucking an acceptable way to get answers.
there are 10,000's of us behind u waiting to hear whether this gene therapy is a partial way home. Most of us are in early and moderate and are precluded from the sample. I would venture to guess is that if they opened the study up to us they would have no problem filling in the dance card.

Your concern is obvious and justified but if I were in the sample the question I would be asking is at what stage in the after surgery observation will I know if the gene therpy is working sufficient enough to open the study up for compassionate reasons.

good luck
gems