In a related development the researchers had come to MJFF prior to the July publication of this finding with the intent to work in advance on a critical next step... we worked to start the development of the needed mouse models with an eye toward open and widespread distribution - ie, a speedy creation of tools that all researchers could quickly access. Read more about this novel way to have science move faster toward therapies.
http://www.pdonlineresearch.org/news...mutation-vps35
Best, Debi